SSIEM 2024
Poster: Pegtibatinase, an Investigational Enzyme Replacement Therapy for Classical Homocystinuria (HCU): Design of the HARMONY and ENSEMBLE Phase 3 Studies
François Maillot; Janet Thomas; Tawfeg Ben-Omran; Harvey Levy; Stephan vom Dahl; Clint Lovell; Sagar A. Vaidya; Can Ficicioglu
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