SIMD 2024

Poster 139: Latest Results from the COMPOSE Phase 1/2 Trial for the Treatment of Classical Homocystinuria (HCU) Using Pegtibatinase, A Novel Investigational Enzyme Replacement Therapy

Jaya Ganesh; Janet Thomas; Wendy E. Smith; Melissa Lah; David Kudrow; Jalé Güner; Sharon McDermott; Sagar A Vaidya; Liz Wilkening; Harvey Levy; Can Ficicioglu

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