GMDI 2024
Poster 33: Novel Dietary Management Strategies for Classical Homocystinuria (HCU) in HARMONY/ENSEMBLE Phase 3 Studies of Pegtibatinase, an Investigational Enzyme Replacement Therapy
Janet Thomas; Tawfeg Ben-Omran; Harvey Levy; Francois Maillot; Stephan vom Dahl; Sharon McDermott; Sergio Slawka; Can Ficicioglu
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